We have created a work environment where our team members support each other, have fun achieving common goals, and feel comfortable being themselves.

We are a global enterprise with opportunities in the United States, Europe, Latin America, and Asia. We offer opportunities of an entrepreneurial biotechnology company working to bring treatments to people with rare genetic diseases for which there is often no existing treatment.

We are looking for people to join our extraordinary team and help us accelerate the development of rare disease therapies to deliver to the people who need them. Come grow with us and find your chance to positively impact the communities we serve.